Orphan Drug – WHAT NEXT

Tag: Orphan Drug

Bile Duct Cancer • Cholangiocarcinoma

September 17, 2024 • Views: 140

FDA Grants Certepetide Orphan Drug Designation For Cholangiocarcinoma

Pancreatic Cancer

June 25, 2024 • Views: 117

Azeliragon Nabs Orphan Drug Designation for Pancreatic Cancer

Acute myeloid leukemia • Leukemia

April 3, 2024 • Views: 184

ICYMI: Ocifisertib Earns Orphan Drug Designation for Acute Myeloid Leukemia

Chronic Myelomonocytic Leukemia • Leukemia

March 18, 2024 • Views: 225

IO-202 for Chronic Myelomonocytic Leukemia (CMML) Earns Orphan Drug Designation

Polycythemia vera

Polycythemia Vera

March 12, 2024 • Views: 184

DISC-3405 for Polycythemia Vera Earns Orphan Drug Designation

Sarcoma • Soft Tissue Sarcoma

March 7, 2024 • Views: 413

Tigilanol Tiglate Granted Orphan Drug Designation for Soft Tissue Sarcoma (STS)

Tenosynovial Giant Cell Tumors

March 12, 2024 • Views: 64

Pimicotinib Earns Orphan Drug Designation from the EMA for Tenosynovial Giant Cell Tumors

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